IJMS | Free Full-Text | An Update on Gene Therapy for Inherited Retinal Dystrophy: Experience in Leber Congenital Amaurosis Clinical Trials
RPE65 gene - Gene Vision
Luxturna: A Gene Therapy Reviving Retinal Cells in Children with Leber Congenital Amaurosis | Arizona RETINA Project
RPE65-related retinal dystrophy: mutational and phenotypic spectrum in 45 affected patients | medRxiv
Gene Therapy for Inherited Retinal Disease
AZ RETINA Project on X: "This happens by restoring the missing enzyme in RPE. The treatment is injected past the neural retina, so it interacts with the RPE. Recently, there has been
RPE65 - retinal degeneration: for patients - Gene Vision
Persistence of non-viral vector mediated RPE65 expression: Case for viability as a gene transfer therapy for RPE-based diseases - ScienceDirect
RPE65 Gene - GeneCards | RPE65 Protein | RPE65 Antibody
RPE65 - Wikipedia
RPE65 - an overview | ScienceDirect Topics
Sequence analysis of the RPE65 gene missense mutation Leu67Arg... | Download Scientific Diagram
Retinal pigment epithelium 65 kDa protein (RPE65): An update - ScienceDirect
Overview of RPE65 mutations reported to date in the Chinese population... | Download Scientific Diagram
Mutations in the RPE65 gene in patients with autosomal recessive retinitis pigmentosa or Leber congenital amaurosis | PNAS
RPE65 gene therapy slows cone loss in Rpe65-deficient dogs | Gene Therapy
Gene therapy in Rpe65 / mice at advanced disease stages leads to... | Download Scientific Diagram
A Gene Scan Study of RPE65 in Chinese Patients with Leber Congenital Amaurosis | Chinese Medical Journal
A Novel Mutation in the RPE65 Gene Causing Leber Congenital Amaurosis and Its Transcriptional Expression In Vitro | PLOS ONE
RPE65 - an overview | ScienceDirect Topics
RPE65 - retinal degeneration: for patients - Gene Vision
Retinal pigment epithelium 65 kDa protein (RPE65): An update - ScienceDirect
RPE65 Gene - GeneCards | RPE65 Protein | RPE65 Antibody
Benefits of gene therapy for both eyes - The Lancet
Luxturna: Gene Therapy for Biallelic RPE65 Mutation-Associated Retinal Dystrophy - YouTube
RPE65 - Wikipedia
A Different Approach to Therapy for Wet AMD
